Genetic modification of somatic stem cells
نویسندگان
چکیده
Some of the illnesses that plague man kind are directly related to our genes. Severe genetic disorders with no current therapeutic options—immuno deficiencies, haemophilia, thalassaemia, muscular dystrophies and cystic fibrosis, for example—could potentially be treated with gene therapy, which uses genetic informa tion to correct a mutation or to provide new functions for human cells. the aim of gene therapy for the past two decades has been to fix the genetic defects in diseased cells of the body, or in the stem cells that can regenerate a diseased tissue or organ.
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